We’re at the Doorstep of a Cure


The Children’s Medical Research Foundation has granted $4.4

million to research a cure for Sanfilippo Syndrome.

About Sanfilippo


Sanfilippo is a rare, neurological disorder that affects roughly 1 in 70,000 births. Research has advanced considerably, but no approved treatment exists, yet.



Your contribution will help fund research and clinical trials of treatments for Sanfilippo Syndrome.

Families make the difference

A cure for Sanfilippo is within reach thanks to countless families inspired by the strength of their courageous children who have battled and continue to fight this disease.

Get In Touch

We’re here for you. Here’s how you can reach us.