We’re at the Doorstep of a Cure
The Children’s Medical Research Foundation has granted $4.4
million to research a cure for Sanfilippo Syndrome.
Sanfilippo is a rare, neurological disorder that affects roughly 1 in 70,000 births. Research has advanced considerably, but no approved treatment exists, yet.
Your contribution will help fund research and clinical trials of treatments for Sanfilippo Syndrome.
Families make the difference
A cure for Sanfilippo is within reach thanks to countless families inspired by the strength of their courageous children who have battled and continue to fight this disease.