We’re at the Doorstep of a Cure


The Children’s Medical Research Foundation has granted $4.25 million to research a cure for Sanfilippo Syndrome.

About Sanfilippo


Sanfilippo is a rare, neurological disorder that affects roughly 1 in 70,000 births. Research has advanced considerably, but no approved treatment exists, yet.



Your contribution will help fund research and clinical trials of treatments for Sanfilippo Syndrome.

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