A cure is here!
We were told it could be done in 1995 and we never looked back!
About Sanfilippo
Sanfilippo is a rare, neurological disorder that affects roughly 1 in 70,000 births. Research has advanced considerably, but no approved treatment exists, yet.
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Your contribution will help fund research and clinical trials of treatments for Sanfilippo Syndrome.
Families make the difference
A cure for Sanfilippo is within reach thanks to countless families inspired by the strength of their courageous children who have battled and continue to fight this disease.